Research Article| Volume 16, ISSUE 1, P197-211, March 1996

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Gene Therapy: A Brief Review

  • Patrick Hess
    Address reprint requests to: Patrick Hess, PhD, 1995 AACC Molecular Pathology Division Chair, Laboratory Corporation of America, 4500 Conaem Drive, Louisville, KY 40213
    From the American Association of Clinical Chemistry Molecular Pathology Division, Laboratory Corporation of America, Louisville, Kentucky
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      This paper is only available as a PDF. To read, Please Download here.
      Gene therapy is no longer defined simply as gene replacement; today, it is better defined as any treatment involving genetic alteration of cells. As a result, its applications have grown enormously and continue to do so. The purpose of gene therapy— treatment of the underlying cause of disease—represents a fundamental break with all previous forms of therapy in the history of medicine. Within a relatively short period, gene therapy promises to be a major pharmacologic force, revolutionizing the practice of medicine.
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